SlideShare uma empresa Scribd logo

Case study cdr p cpa re kuvan for cord november 2015

•
•
Canadian Organization for Rare Disorders
Canadian Organization for Rare Disorders

Expert Patient Advocates & 21st Century Therapies Forum Nov 19 - 20, 2015

Saúde e medicina
1 de 11
Baixar para ler offline
Case Study of Common Drug Review & pan-Canadian Pharmaceutical Alliance and the first drug for PKU: restrictive criteria = no access John Adams President & CEO Canadian PKU and Allied Disorders Inc. (CanPKU) November 20, 2015 CORD Expert Patients conference
PKU 101 PKU stands for Phenylketonuria: •  a rare, genetic disorder •  brain-threatening •  intellectual disabilities, seizures & other neurologic problems •  incidence in Canada: 1:12,000 •  every newborn in Canada is tested for PKU since 1960s •  only treatment since 1950s: - vegan diet without natural protein - synthetic protein (formulas & low-protein foods) - lifetime treatment, only since 2000 CanPKU Role: •  improve lives of people living with PKU and their families •  founded 2008: peer support, knowledge transfer, advocacy
Why do we need a drug for PKU? PKU diet is very restrictive and hard to manage Francjan van Spronsen, MD, PhD, chair of scientific advisory committee of the European Society for PKU - Presenting Oct. 24, 2015
Government Reimbursement for first drug for PKU Overview: 2010: Health Canada approves Drug company applies to CDR Drug company asks for reconsideration on seeing confidential draft report CEDC says Do Not List – special note! 2011: Provinces submit request for advice to clarify special note CEDC does not change recommendation or special note 2012: ON, SK and BC negotiate with drug company; BC in lead 2013: ON & SK list drug with strict criteria: BC drops out 2014-15: SK & ON refuse eight applications 2015: ON for pCPA says drug must go back to CDR
Access to Kuvan™ today Private •  private insurance •  clinical trials •  compassionate access by drug company Governments •  Listed in ON & SK: zero patients •  Listed in QC: eight patients •  Health Canada: two patients (aboriginals) •  Alberta: two patients (disabled)
Ontario MD specialists criticized Govt criteria
pCPA Current Position 1.  No change in access criteria and no province will negotiate individually 2.  Drug company must submit new clinical information to CDR – fourth trip to CEDC since 2010 3.  Only if a positive CDR/CDEC recommendation, then pCPA will negotiate
Case study cdr p cpa re kuvan for cord november 2015
Case study cdr p cpa re kuvan for cord november 2015

Recomendados

Barbara Sabourin regulating drugs in canada v2
Barbara Sabourin regulating drugs in canada v2Barbara Sabourin regulating drugs in canada v2
Barbara Sabourin regulating drugs in canada v2Canadian Organization for Rare Disorders
 
Your input on the Goals Feedback, metrics and priority actions
Your input on the Goals Feedback, metrics and priority actionsYour input on the Goals Feedback, metrics and priority actions
Your input on the Goals Feedback, metrics and priority actionsCanadian Organization for Rare Disorders
 
Oncology Dynamics - IQVIA
Oncology Dynamics - IQVIAOncology Dynamics - IQVIA
Oncology Dynamics - IQVIAWeronika Ficek
 
STREAM ONE: Donna Wall, Bone marrow as a Vehicle for Correction of Rare Disor...
STREAM ONE: Donna Wall, Bone marrow as a Vehicle for Correction of Rare Disor...STREAM ONE: Donna Wall, Bone marrow as a Vehicle for Correction of Rare Disor...
STREAM ONE: Donna Wall, Bone marrow as a Vehicle for Correction of Rare Disor...Canadian Organization for Rare Disorders
 
RWD/RWE for Rare Disease Drugs Webinar
RWD/RWE for Rare Disease Drugs WebinarRWD/RWE for Rare Disease Drugs Webinar
RWD/RWE for Rare Disease Drugs WebinarCanadian Organization for Rare Disorders
 
Rare Disorders Policies in Canada: Who’s who and what’s what
Rare Disorders Policies in Canada: Who’s who and what’s whatRare Disorders Policies in Canada: Who’s who and what’s what
Rare Disorders Policies in Canada: Who’s who and what’s whatCanadian Organization for Rare Disorders
 
Effective Patient Advocacy: Problem + Solution = Collaboration
Effective Patient Advocacy: Problem + Solution = CollaborationEffective Patient Advocacy: Problem + Solution = Collaboration
Effective Patient Advocacy: Problem + Solution = CollaborationCanadian Organization for Rare Disorders
 
Patient Input: What is asked for and what is helpful in a patient submission
Patient Input: What is asked for and what is helpful in a patient submissionPatient Input: What is asked for and what is helpful in a patient submission
Patient Input: What is asked for and what is helpful in a patient submissionCanadian Organization for Rare Disorders
 

Recomendados

Barbara Sabourin regulating drugs in canada v2
Barbara Sabourin regulating drugs in canada v2Barbara Sabourin regulating drugs in canada v2
Barbara Sabourin regulating drugs in canada v2Canadian Organization for Rare Disorders
 
Your input on the Goals Feedback, metrics and priority actions
Your input on the Goals Feedback, metrics and priority actionsYour input on the Goals Feedback, metrics and priority actions
Your input on the Goals Feedback, metrics and priority actionsCanadian Organization for Rare Disorders
 
Oncology Dynamics - IQVIA
Oncology Dynamics - IQVIAOncology Dynamics - IQVIA
Oncology Dynamics - IQVIAWeronika Ficek
 
STREAM ONE: Donna Wall, Bone marrow as a Vehicle for Correction of Rare Disor...
STREAM ONE: Donna Wall, Bone marrow as a Vehicle for Correction of Rare Disor...STREAM ONE: Donna Wall, Bone marrow as a Vehicle for Correction of Rare Disor...
STREAM ONE: Donna Wall, Bone marrow as a Vehicle for Correction of Rare Disor...Canadian Organization for Rare Disorders
 
RWD/RWE for Rare Disease Drugs Webinar
RWD/RWE for Rare Disease Drugs WebinarRWD/RWE for Rare Disease Drugs Webinar
RWD/RWE for Rare Disease Drugs WebinarCanadian Organization for Rare Disorders
 
Rare Disorders Policies in Canada: Who’s who and what’s what
Rare Disorders Policies in Canada: Who’s who and what’s whatRare Disorders Policies in Canada: Who’s who and what’s what
Rare Disorders Policies in Canada: Who’s who and what’s whatCanadian Organization for Rare Disorders
 
Effective Patient Advocacy: Problem + Solution = Collaboration
Effective Patient Advocacy: Problem + Solution = CollaborationEffective Patient Advocacy: Problem + Solution = Collaboration
Effective Patient Advocacy: Problem + Solution = CollaborationCanadian Organization for Rare Disorders
 
Patient Input: What is asked for and what is helpful in a patient submission
Patient Input: What is asked for and what is helpful in a patient submissionPatient Input: What is asked for and what is helpful in a patient submission
Patient Input: What is asked for and what is helpful in a patient submissionCanadian Organization for Rare Disorders
 
Durhane: Rare Drug Strategy Webinar
Durhane: Rare Drug Strategy WebinarDurhane: Rare Drug Strategy Webinar
Durhane: Rare Drug Strategy WebinarCanadian Organization for Rare Disorders
 
Patient Group Development and Engagement
Patient Group Development and EngagementPatient Group Development and Engagement
Patient Group Development and EngagementCanadian Organization for Rare Disorders
 
Cathy parker the orphan drug framework
Cathy parker the orphan drug frameworkCathy parker the orphan drug framework
Cathy parker the orphan drug frameworkCanadian Organization for Rare Disorders
 
Durhane Wong-Rieger (CORD) Canada's Rare Disease Strategy Brief Overview
Durhane Wong-Rieger (CORD) Canada's Rare Disease Strategy Brief Overview Durhane Wong-Rieger (CORD) Canada's Rare Disease Strategy Brief Overview
Durhane Wong-Rieger (CORD) Canada's Rare Disease Strategy Brief Overview Canadian Organization for Rare Disorders
 
Glenn Monteith expert patients forum
Glenn Monteith expert patients forumGlenn Monteith expert patients forum
Glenn Monteith expert patients forumCanadian Organization for Rare Disorders
 
Chander slides november 19 20 2015-toronto
Chander slides november 19 20 2015-torontoChander slides november 19 20 2015-toronto
Chander slides november 19 20 2015-torontoCanadian Organization for Rare Disorders
 
Dr. Greenberg CORD Mar 23-24, 2022 Rare Drug Strategy WebinarDay
Dr. Greenberg CORD Mar 23-24, 2022 Rare Drug Strategy WebinarDayDr. Greenberg CORD Mar 23-24, 2022 Rare Drug Strategy WebinarDay
Dr. Greenberg CORD Mar 23-24, 2022 Rare Drug Strategy WebinarDayCanadian Organization for Rare Disorders
 
STREAM THREE: Jeff Keefer, Inclusion in Clinical Trials
STREAM THREE: Jeff Keefer, Inclusion in Clinical Trials STREAM THREE: Jeff Keefer, Inclusion in Clinical Trials
STREAM THREE: Jeff Keefer, Inclusion in Clinical Trials Canadian Organization for Rare Disorders
 
David page cord standards of care 05 03-2015
David page cord standards of care 05 03-2015David page cord standards of care 05 03-2015
David page cord standards of care 05 03-2015Canadian Organization for Rare Disorders
 
Vers une Stratégie québécoise en matière de maladies rares
Vers une Stratégie québécoise en matière de maladies raresVers une Stratégie québécoise en matière de maladies rares
Vers une Stratégie québécoise en matière de maladies raresCanadian Organization for Rare Disorders
 
Access to Drugs for Rare Diseases in Canada - April 2014
Access to Drugs for Rare Diseases in Canada - April 2014Access to Drugs for Rare Diseases in Canada - April 2014
Access to Drugs for Rare Diseases in Canada - April 2014Canadian Organization for Rare Disorders
 
Rare Disease Day Conference: From Draft to Action Plan
Rare Disease Day Conference: From Draft to Action PlanRare Disease Day Conference: From Draft to Action Plan
Rare Disease Day Conference: From Draft to Action PlanCanadian Organization for Rare Disorders
 
Canada’s Orphan Drug Regulatory Framework & panCanadian Access to Rare Diseas...
Canada’s Orphan Drug Regulatory Framework & panCanadian Access to Rare Diseas...Canada’s Orphan Drug Regulatory Framework & panCanadian Access to Rare Diseas...
Canada’s Orphan Drug Regulatory Framework & panCanadian Access to Rare Diseas...Canadian Organization for Rare Disorders
 
Canada’s Orphan Drug Regulatory Framework & panCanadian Access to Rare Diseas...
Canada’s Orphan Drug Regulatory Framework & panCanadian Access to Rare Diseas...Canada’s Orphan Drug Regulatory Framework & panCanadian Access to Rare Diseas...
Canada’s Orphan Drug Regulatory Framework & panCanadian Access to Rare Diseas...Canadian Organization for Rare Disorders
 
Matt Bolz-Johnson: Rare Drug Strategy Webinar
Matt Bolz-Johnson: Rare Drug Strategy Webinar Matt Bolz-Johnson: Rare Drug Strategy Webinar
Matt Bolz-Johnson: Rare Drug Strategy Webinar Canadian Organization for Rare Disorders
 
Clinical Trials on Repurposed Treatments for Immediate Incorporation into Cli...
Clinical Trials on Repurposed Treatments for Immediate Incorporation into Cli...Clinical Trials on Repurposed Treatments for Immediate Incorporation into Cli...
Clinical Trials on Repurposed Treatments for Immediate Incorporation into Cli...Canadian Organization for Rare Disorders
 
Hta barriers to ideal
Hta barriers to idealHta barriers to ideal
Hta barriers to idealCanadian Organization for Rare Disorders
 
Multidisciplinary teams for diagnosis and treatment of children (and adults) ...
Multidisciplinary teams for diagnosis and treatment of children (and adults) ...Multidisciplinary teams for diagnosis and treatment of children (and adults) ...
Multidisciplinary teams for diagnosis and treatment of children (and adults) ...Canadian Organization for Rare Disorders
 
Advances in Rare Disease Gareth Baynam, Western Australia Health Department (...
Advances in Rare Disease Gareth Baynam, Western Australia Health Department (...Advances in Rare Disease Gareth Baynam, Western Australia Health Department (...
Advances in Rare Disease Gareth Baynam, Western Australia Health Department (...Canadian Organization for Rare Disorders
 
Michael reilly toronto nov19presentation final
Michael reilly toronto nov19presentation finalMichael reilly toronto nov19presentation final
Michael reilly toronto nov19presentation finalCanadian Organization for Rare Disorders
 
Does Canada need an Orphan Drug Policy to incentivize drug development and su...
Does Canada need an Orphan Drug Policy to incentivize drug development and su...Does Canada need an Orphan Drug Policy to incentivize drug development and su...
Does Canada need an Orphan Drug Policy to incentivize drug development and su...Canadian Organization for Rare Disorders
 
CCSN Advocacy Webinar #2
CCSN Advocacy Webinar #2CCSN Advocacy Webinar #2
CCSN Advocacy Webinar #2Tiffany Glover
 

Mais conteúdo relacionado

Mais procurados

Canada’s Orphan Drug Regulatory Framework & panCanadian Access to Rare Diseas...
Canada’s Orphan Drug Regulatory Framework & panCanadian Access to Rare Diseas...Canada’s Orphan Drug Regulatory Framework & panCanadian Access to Rare Diseas...
Canada’s Orphan Drug Regulatory Framework & panCanadian Access to Rare Diseas...Canadian Organization for Rare Disorders
 
Canada’s Orphan Drug Regulatory Framework & panCanadian Access to Rare Diseas...
Canada’s Orphan Drug Regulatory Framework & panCanadian Access to Rare Diseas...Canada’s Orphan Drug Regulatory Framework & panCanadian Access to Rare Diseas...
Canada’s Orphan Drug Regulatory Framework & panCanadian Access to Rare Diseas...Canadian Organization for Rare Disorders
 
Clinical Trials on Repurposed Treatments for Immediate Incorporation into Cli...
Clinical Trials on Repurposed Treatments for Immediate Incorporation into Cli...Clinical Trials on Repurposed Treatments for Immediate Incorporation into Cli...
Clinical Trials on Repurposed Treatments for Immediate Incorporation into Cli...Canadian Organization for Rare Disorders
 
Multidisciplinary teams for diagnosis and treatment of children (and adults) ...
Multidisciplinary teams for diagnosis and treatment of children (and adults) ...Multidisciplinary teams for diagnosis and treatment of children (and adults) ...
Multidisciplinary teams for diagnosis and treatment of children (and adults) ...Canadian Organization for Rare Disorders
 
Advances in Rare Disease Gareth Baynam, Western Australia Health Department (...
Advances in Rare Disease Gareth Baynam, Western Australia Health Department (...Advances in Rare Disease Gareth Baynam, Western Australia Health Department (...
Advances in Rare Disease Gareth Baynam, Western Australia Health Department (...Canadian Organization for Rare Disorders
 

Mais procurados (20)

Durhane: Rare Drug Strategy Webinar
Durhane: Rare Drug Strategy WebinarDurhane: Rare Drug Strategy Webinar
Durhane: Rare Drug Strategy Webinar
 
Patient Group Development and Engagement
Patient Group Development and EngagementPatient Group Development and Engagement
Patient Group Development and Engagement
 
Cathy parker the orphan drug framework
Cathy parker the orphan drug frameworkCathy parker the orphan drug framework
Cathy parker the orphan drug framework
 
Durhane Wong-Rieger (CORD) Canada's Rare Disease Strategy Brief Overview
Durhane Wong-Rieger (CORD) Canada's Rare Disease Strategy Brief Overview Durhane Wong-Rieger (CORD) Canada's Rare Disease Strategy Brief Overview
Durhane Wong-Rieger (CORD) Canada's Rare Disease Strategy Brief Overview
 
Glenn Monteith expert patients forum
Glenn Monteith expert patients forumGlenn Monteith expert patients forum
Glenn Monteith expert patients forum
 
Chander slides november 19 20 2015-toronto
Chander slides november 19 20 2015-torontoChander slides november 19 20 2015-toronto
Chander slides november 19 20 2015-toronto
 
Dr. Greenberg CORD Mar 23-24, 2022 Rare Drug Strategy WebinarDay
Dr. Greenberg CORD Mar 23-24, 2022 Rare Drug Strategy WebinarDayDr. Greenberg CORD Mar 23-24, 2022 Rare Drug Strategy WebinarDay
Dr. Greenberg CORD Mar 23-24, 2022 Rare Drug Strategy WebinarDay
 
STREAM THREE: Jeff Keefer, Inclusion in Clinical Trials
STREAM THREE: Jeff Keefer, Inclusion in Clinical Trials STREAM THREE: Jeff Keefer, Inclusion in Clinical Trials
STREAM THREE: Jeff Keefer, Inclusion in Clinical Trials
 
David page cord standards of care 05 03-2015
David page cord standards of care 05 03-2015David page cord standards of care 05 03-2015
David page cord standards of care 05 03-2015
 
Vers une Stratégie québécoise en matière de maladies rares
Vers une Stratégie québécoise en matière de maladies raresVers une Stratégie québécoise en matière de maladies rares
Vers une Stratégie québécoise en matière de maladies rares
 
Access to Drugs for Rare Diseases in Canada - April 2014
Access to Drugs for Rare Diseases in Canada - April 2014Access to Drugs for Rare Diseases in Canada - April 2014
Access to Drugs for Rare Diseases in Canada - April 2014
 
Rare Disease Day Conference: From Draft to Action Plan
Rare Disease Day Conference: From Draft to Action PlanRare Disease Day Conference: From Draft to Action Plan
Rare Disease Day Conference: From Draft to Action Plan
 
Canada’s Orphan Drug Regulatory Framework & panCanadian Access to Rare Diseas...
Canada’s Orphan Drug Regulatory Framework & panCanadian Access to Rare Diseas...Canada’s Orphan Drug Regulatory Framework & panCanadian Access to Rare Diseas...
Canada’s Orphan Drug Regulatory Framework & panCanadian Access to Rare Diseas...
 
Canada’s Orphan Drug Regulatory Framework & panCanadian Access to Rare Diseas...
Canada’s Orphan Drug Regulatory Framework & panCanadian Access to Rare Diseas...Canada’s Orphan Drug Regulatory Framework & panCanadian Access to Rare Diseas...
Canada’s Orphan Drug Regulatory Framework & panCanadian Access to Rare Diseas...
 
Matt Bolz-Johnson: Rare Drug Strategy Webinar
Matt Bolz-Johnson: Rare Drug Strategy Webinar Matt Bolz-Johnson: Rare Drug Strategy Webinar
Matt Bolz-Johnson: Rare Drug Strategy Webinar
 
Clinical Trials on Repurposed Treatments for Immediate Incorporation into Cli...
Clinical Trials on Repurposed Treatments for Immediate Incorporation into Cli...Clinical Trials on Repurposed Treatments for Immediate Incorporation into Cli...
Clinical Trials on Repurposed Treatments for Immediate Incorporation into Cli...
 
Hta barriers to ideal
Hta barriers to idealHta barriers to ideal
Hta barriers to ideal
 
Multidisciplinary teams for diagnosis and treatment of children (and adults) ...
Multidisciplinary teams for diagnosis and treatment of children (and adults) ...Multidisciplinary teams for diagnosis and treatment of children (and adults) ...
Multidisciplinary teams for diagnosis and treatment of children (and adults) ...
 
Advances in Rare Disease Gareth Baynam, Western Australia Health Department (...
Advances in Rare Disease Gareth Baynam, Western Australia Health Department (...Advances in Rare Disease Gareth Baynam, Western Australia Health Department (...
Advances in Rare Disease Gareth Baynam, Western Australia Health Department (...
 
Michael reilly toronto nov19presentation final
Michael reilly toronto nov19presentation finalMichael reilly toronto nov19presentation final
Michael reilly toronto nov19presentation final
 

Semelhante a Case study cdr p cpa re kuvan for cord november 2015

Does Canada need an Orphan Drug Policy to incentivize drug development and su...
Does Canada need an Orphan Drug Policy to incentivize drug development and su...Does Canada need an Orphan Drug Policy to incentivize drug development and su...
Does Canada need an Orphan Drug Policy to incentivize drug development and su...Canadian Organization for Rare Disorders
 
CCSN Advocacy Webinar #2
CCSN Advocacy Webinar #2CCSN Advocacy Webinar #2
CCSN Advocacy Webinar #2Tiffany Glover
 
Market Access Climate Change Webinar_the Evolving Impact of Product Listing A...
Market Access Climate Change Webinar_the Evolving Impact of Product Listing A...Market Access Climate Change Webinar_the Evolving Impact of Product Listing A...
Market Access Climate Change Webinar_the Evolving Impact of Product Listing A...Arvind Mani
 
Bringing Rare Disease Drugs to Canada Opportunities, Challenges, and More Cha...
Bringing Rare Disease Drugs to Canada Opportunities, Challenges, and More Cha...Bringing Rare Disease Drugs to Canada Opportunities, Challenges, and More Cha...
Bringing Rare Disease Drugs to Canada Opportunities, Challenges, and More Cha...Canadian Cancer Survivor Network
 
Drug Approval Bodies in Canada 101: The Elevator Length Pitch
Drug Approval Bodies in Canada 101: The Elevator Length PitchDrug Approval Bodies in Canada 101: The Elevator Length Pitch
Drug Approval Bodies in Canada 101: The Elevator Length PitchCanadian Cancer Survivor Network
 
Weitzman ECHO: Challenges in Addressing the Evolving Opioid Crisis During COV...
Weitzman ECHO: Challenges in Addressing the Evolving Opioid Crisis During COV...Weitzman ECHO: Challenges in Addressing the Evolving Opioid Crisis During COV...
Weitzman ECHO: Challenges in Addressing the Evolving Opioid Crisis During COV...CHC Connecticut
 
Challenges and Innovation in Canadian Access to Treatments and Innovation
Challenges and Innovation in Canadian Access to Treatments and InnovationChallenges and Innovation in Canadian Access to Treatments and Innovation
Challenges and Innovation in Canadian Access to Treatments and InnovationCanadian Cancer Survivor Network
 
Virginia Llera - Cómo optimizar la investigación en Enfermedades Raras
Virginia Llera - Cómo optimizar la investigación en Enfermedades RarasVirginia Llera - Cómo optimizar la investigación en Enfermedades Raras
Virginia Llera - Cómo optimizar la investigación en Enfermedades RarasFundación Ramón Areces
 
Cadth 2015 c6 panel collab formulary hospital-public plan - eric lun final
Cadth 2015 c6 panel collab formulary hospital-public plan - eric lun finalCadth 2015 c6 panel collab formulary hospital-public plan - eric lun final
Cadth 2015 c6 panel collab formulary hospital-public plan - eric lun finalCADTH Symposium
 
STREAM TWO: Fiona Frappier, Canada’s regulatory approach to drugs for rare di...
STREAM TWO: Fiona Frappier, Canada’s regulatory approach to drugs for rare di...STREAM TWO: Fiona Frappier, Canada’s regulatory approach to drugs for rare di...
STREAM TWO: Fiona Frappier, Canada’s regulatory approach to drugs for rare di...Canadian Organization for Rare Disorders
 
Unpacking the OHIP+ pharmacare plan for kids & youth in Ontario
Unpacking the OHIP+ pharmacare plan for kids & youth in OntarioUnpacking the OHIP+ pharmacare plan for kids & youth in Ontario
Unpacking the OHIP+ pharmacare plan for kids & youth in OntarioCanadian Cancer Survivor Network
 
Clinical pharmacy– a key role
Clinical pharmacy– a key roleClinical pharmacy– a key role
Clinical pharmacy– a key roleNursing Hi Nursing
 
International Medical Cannabis Policy - Philippe Lucas (Canada)
International Medical Cannabis Policy - Philippe Lucas (Canada) International Medical Cannabis Policy - Philippe Lucas (Canada)
International Medical Cannabis Policy - Philippe Lucas (Canada) SafeAccess
 
Jodie: A Health Consumer Perspective
Jodie: A Health Consumer PerspectiveJodie: A Health Consumer Perspective
Jodie: A Health Consumer PerspectiveJodiesjourneycom
 

Semelhante a Case study cdr p cpa re kuvan for cord november 2015 (20)

Does Canada need an Orphan Drug Policy to incentivize drug development and su...
Does Canada need an Orphan Drug Policy to incentivize drug development and su...Does Canada need an Orphan Drug Policy to incentivize drug development and su...
Does Canada need an Orphan Drug Policy to incentivize drug development and su...
 
CCSN Advocacy Webinar #2
CCSN Advocacy Webinar #2CCSN Advocacy Webinar #2
CCSN Advocacy Webinar #2
 
CBoC_IMC_Time to Patient Presentation_CCSN.pdf
CBoC_IMC_Time to Patient Presentation_CCSN.pdfCBoC_IMC_Time to Patient Presentation_CCSN.pdf
CBoC_IMC_Time to Patient Presentation_CCSN.pdf
 
The Cancer Medication Geographical Roulette in Canada
The Cancer Medication Geographical Roulette in CanadaThe Cancer Medication Geographical Roulette in Canada
The Cancer Medication Geographical Roulette in Canada
 
Rare Disease access issues 2015 v2
Rare Disease access issues 2015 v2Rare Disease access issues 2015 v2
Rare Disease access issues 2015 v2
 
Orphan Drugs
Orphan DrugsOrphan Drugs
Orphan Drugs
 
Examining Models for a National Pharmacare Program
Examining Models for a National Pharmacare ProgramExamining Models for a National Pharmacare Program
Examining Models for a National Pharmacare Program
 
Market Access Climate Change Webinar_the Evolving Impact of Product Listing A...
Market Access Climate Change Webinar_the Evolving Impact of Product Listing A...Market Access Climate Change Webinar_the Evolving Impact of Product Listing A...
Market Access Climate Change Webinar_the Evolving Impact of Product Listing A...
 
Bringing Rare Disease Drugs to Canada Opportunities, Challenges, and More Cha...
Bringing Rare Disease Drugs to Canada Opportunities, Challenges, and More Cha...Bringing Rare Disease Drugs to Canada Opportunities, Challenges, and More Cha...
Bringing Rare Disease Drugs to Canada Opportunities, Challenges, and More Cha...
 
Drug Approval Bodies in Canada 101: The Elevator Length Pitch
Drug Approval Bodies in Canada 101: The Elevator Length PitchDrug Approval Bodies in Canada 101: The Elevator Length Pitch
Drug Approval Bodies in Canada 101: The Elevator Length Pitch
 
Weitzman ECHO: Challenges in Addressing the Evolving Opioid Crisis During COV...
Weitzman ECHO: Challenges in Addressing the Evolving Opioid Crisis During COV...Weitzman ECHO: Challenges in Addressing the Evolving Opioid Crisis During COV...
Weitzman ECHO: Challenges in Addressing the Evolving Opioid Crisis During COV...
 
Challenges and Innovation in Canadian Access to Treatments and Innovation
Challenges and Innovation in Canadian Access to Treatments and InnovationChallenges and Innovation in Canadian Access to Treatments and Innovation
Challenges and Innovation in Canadian Access to Treatments and Innovation
 
Virginia Llera - Cómo optimizar la investigación en Enfermedades Raras
Virginia Llera - Cómo optimizar la investigación en Enfermedades RarasVirginia Llera - Cómo optimizar la investigación en Enfermedades Raras
Virginia Llera - Cómo optimizar la investigación en Enfermedades Raras
 
Cadth 2015 c6 panel collab formulary hospital-public plan - eric lun final
Cadth 2015 c6 panel collab formulary hospital-public plan - eric lun finalCadth 2015 c6 panel collab formulary hospital-public plan - eric lun final
Cadth 2015 c6 panel collab formulary hospital-public plan - eric lun final
 
STREAM TWO: Fiona Frappier, Canada’s regulatory approach to drugs for rare di...
STREAM TWO: Fiona Frappier, Canada’s regulatory approach to drugs for rare di...STREAM TWO: Fiona Frappier, Canada’s regulatory approach to drugs for rare di...
STREAM TWO: Fiona Frappier, Canada’s regulatory approach to drugs for rare di...
 
Unpacking the OHIP+ pharmacare plan for kids & youth in Ontario
Unpacking the OHIP+ pharmacare plan for kids & youth in OntarioUnpacking the OHIP+ pharmacare plan for kids & youth in Ontario
Unpacking the OHIP+ pharmacare plan for kids & youth in Ontario
 
Clinical pharmacy– a key role
Clinical pharmacy– a key roleClinical pharmacy– a key role
Clinical pharmacy– a key role
 
International Medical Cannabis Policy - Philippe Lucas (Canada)
International Medical Cannabis Policy - Philippe Lucas (Canada) International Medical Cannabis Policy - Philippe Lucas (Canada)
International Medical Cannabis Policy - Philippe Lucas (Canada)
 
Pharmacare 2.0 initiative
Pharmacare 2.0 initiativePharmacare 2.0 initiative
Pharmacare 2.0 initiative
 
Jodie: A Health Consumer Perspective
Jodie: A Health Consumer PerspectiveJodie: A Health Consumer Perspective
Jodie: A Health Consumer Perspective
 

Mais de Canadian Organization for Rare Disorders

Day 2: Thierry Lacaze-Masmonteil, Maternal Infant Child Youth Research Network
Day 2: Thierry Lacaze-Masmonteil, Maternal Infant Child Youth Research NetworkDay 2: Thierry Lacaze-Masmonteil, Maternal Infant Child Youth Research Network
Day 2: Thierry Lacaze-Masmonteil, Maternal Infant Child Youth Research NetworkCanadian Organization for Rare Disorders
 
Day 2: Cheryl Greenberg, Children's Hospital Research Institute of Manitoba
Day 2: Cheryl Greenberg, Children's Hospital Research Institute of ManitobaDay 2: Cheryl Greenberg, Children's Hospital Research Institute of Manitoba
Day 2: Cheryl Greenberg, Children's Hospital Research Institute of ManitobaCanadian Organization for Rare Disorders
 
Day 1: INFORM RARE: Beth Potter, Alexandra Wyatt, Pranesh Chakraborty, Monica...
Day 1: INFORM RARE: Beth Potter, Alexandra Wyatt, Pranesh Chakraborty, Monica...Day 1: INFORM RARE: Beth Potter, Alexandra Wyatt, Pranesh Chakraborty, Monica...
Day 1: INFORM RARE: Beth Potter, Alexandra Wyatt, Pranesh Chakraborty, Monica...Canadian Organization for Rare Disorders
 
Day 1 : Canadian Neuromuscular Network, Western University - Craig Campbell, ...
Day 1 : Canadian Neuromuscular Network, Western University - Craig Campbell, ...Day 1 : Canadian Neuromuscular Network, Western University - Craig Campbell, ...
Day 1 : Canadian Neuromuscular Network, Western University - Craig Campbell, ...Canadian Organization for Rare Disorders
 
Day 1: Rare Disease Research Network and National Children’s Hospital - Marsh...
Day 1: Rare Disease Research Network and National Children’s Hospital - Marsh...Day 1: Rare Disease Research Network and National Children’s Hospital - Marsh...
Day 1: Rare Disease Research Network and National Children’s Hospital - Marsh...Canadian Organization for Rare Disorders
 

Mais de Canadian Organization for Rare Disorders (20)

Webinar: Investing $1.5b in A Sustainable Rare Disease Ecosystem
Webinar: Investing $1.5b in A Sustainable Rare Disease EcosystemWebinar: Investing $1.5b in A Sustainable Rare Disease Ecosystem
Webinar: Investing $1.5b in A Sustainable Rare Disease Ecosystem
 
CORD-RQMO: English Slides
CORD-RQMO: English Slides CORD-RQMO: English Slides
CORD-RQMO: English Slides
 
CORD-RQMO: French Slides
CORD-RQMO: French SlidesCORD-RQMO: French Slides
CORD-RQMO: French Slides
 
Webinar: PMPRB NEW Guidelines and Impact on Rare Diseases
Webinar: PMPRB NEW Guidelines and Impact on Rare Diseases Webinar: PMPRB NEW Guidelines and Impact on Rare Diseases
Webinar: PMPRB NEW Guidelines and Impact on Rare Diseases
 
Day 1: NORD Centres of Excellence - Pamela Gavin
Day 1: NORD Centres of Excellence - Pamela GavinDay 1: NORD Centres of Excellence - Pamela Gavin
Day 1: NORD Centres of Excellence - Pamela Gavin
 
Day 1: IAM RARE: Pamela Gavin, NORD
Day 1: IAM RARE: Pamela Gavin, NORDDay 1: IAM RARE: Pamela Gavin, NORD
Day 1: IAM RARE: Pamela Gavin, NORD
 
Day 2: Rare Disease & Drug Access Pathway
Day 2: Rare Disease & Drug Access Pathway Day 2: Rare Disease & Drug Access Pathway
Day 2: Rare Disease & Drug Access Pathway
 
Day 2: Thierry Lacaze-Masmonteil, Maternal Infant Child Youth Research Network
Day 2: Thierry Lacaze-Masmonteil, Maternal Infant Child Youth Research NetworkDay 2: Thierry Lacaze-Masmonteil, Maternal Infant Child Youth Research Network
Day 2: Thierry Lacaze-Masmonteil, Maternal Infant Child Youth Research Network
 
Dar 2: Patient Engagement and Patient Empowerment Panel
Dar 2: Patient Engagement and Patient Empowerment Panel Dar 2: Patient Engagement and Patient Empowerment Panel
Dar 2: Patient Engagement and Patient Empowerment Panel
 
Day 2: Cheryl Greenberg, Children's Hospital Research Institute of Manitoba
Day 2: Cheryl Greenberg, Children's Hospital Research Institute of ManitobaDay 2: Cheryl Greenberg, Children's Hospital Research Institute of Manitoba
Day 2: Cheryl Greenberg, Children's Hospital Research Institute of Manitoba
 
Day 1: INFORM RARE: Beth Potter, Alexandra Wyatt, Pranesh Chakraborty, Monica...
Day 1: INFORM RARE: Beth Potter, Alexandra Wyatt, Pranesh Chakraborty, Monica...Day 1: INFORM RARE: Beth Potter, Alexandra Wyatt, Pranesh Chakraborty, Monica...
Day 1: INFORM RARE: Beth Potter, Alexandra Wyatt, Pranesh Chakraborty, Monica...
 
Day 1: Newborn Screening: Pranesh Chakraborty, University of Ottawa
Day 1: Newborn Screening: Pranesh Chakraborty, University of OttawaDay 1: Newborn Screening: Pranesh Chakraborty, University of Ottawa
Day 1: Newborn Screening: Pranesh Chakraborty, University of Ottawa
 
Day 1: Phenotypes: Orion Buske, PhenoTips
Day 1: Phenotypes: Orion Buske, PhenoTipsDay 1: Phenotypes: Orion Buske, PhenoTips
Day 1: Phenotypes: Orion Buske, PhenoTips
 
Day 1: Genomic Sequencing: Kym Boycott, CHEO
Day 1: Genomic Sequencing: Kym Boycott, CHEODay 1: Genomic Sequencing: Kym Boycott, CHEO
Day 1: Genomic Sequencing: Kym Boycott, CHEO
 
Day 1: INFORM RARE
Day 1: INFORM RAREDay 1: INFORM RARE
Day 1: INFORM RARE
 
Day 1 : Canadian Neuromuscular Network, Western University - Craig Campbell, ...
Day 1 : Canadian Neuromuscular Network, Western University - Craig Campbell, ...Day 1 : Canadian Neuromuscular Network, Western University - Craig Campbell, ...
Day 1 : Canadian Neuromuscular Network, Western University - Craig Campbell, ...
 
Day 1: Rare Disease Research Network and National Children’s Hospital - Marsh...
Day 1: Rare Disease Research Network and National Children’s Hospital - Marsh...Day 1: Rare Disease Research Network and National Children’s Hospital - Marsh...
Day 1: Rare Disease Research Network and National Children’s Hospital - Marsh...
 
Day 1: WHO-RDI Global Rare Disease Network - Matt Bolz-Johnson, EURORDIS
Day 1: WHO-RDI Global Rare Disease Network - Matt Bolz-Johnson, EURORDISDay 1: WHO-RDI Global Rare Disease Network - Matt Bolz-Johnson, EURORDIS
Day 1: WHO-RDI Global Rare Disease Network - Matt Bolz-Johnson, EURORDIS
 
Day 1: Children's Healthcare Canada CORD
Day 1: Children's Healthcare Canada CORD Day 1: Children's Healthcare Canada CORD
Day 1: Children's Healthcare Canada CORD
 
Day 1: Network of Centres of Excellence
Day 1: Network of Centres of ExcellenceDay 1: Network of Centres of Excellence
Day 1: Network of Centres of Excellence
 

Último

♛VVIP Hyderabad Call Girls Chintalkunta🖕7001035870🖕Riya Kappor Top Call Girl ...
♛VVIP Hyderabad Call Girls Chintalkunta🖕7001035870🖕Riya Kappor Top Call Girl ...♛VVIP Hyderabad Call Girls Chintalkunta🖕7001035870🖕Riya Kappor Top Call Girl ...
♛VVIP Hyderabad Call Girls Chintalkunta🖕7001035870🖕Riya Kappor Top Call Girl ...astropune
 
Top Rated Bangalore Call Girls Richmond Circle ⟟ 9332606886 ⟟ Call Me For Ge...
Top Rated Bangalore Call Girls Richmond Circle ⟟ 9332606886 ⟟ Call Me For Ge...Top Rated Bangalore Call Girls Richmond Circle ⟟ 9332606886 ⟟ Call Me For Ge...
Top Rated Bangalore Call Girls Richmond Circle ⟟ 9332606886 ⟟ Call Me For Ge...narwatsonia7
 
Call Girls Gwalior Just Call 8617370543 Top Class Call Girl Service Available
Call Girls Gwalior Just Call 8617370543 Top Class Call Girl Service AvailableCall Girls Gwalior Just Call 8617370543 Top Class Call Girl Service Available
Call Girls Gwalior Just Call 8617370543 Top Class Call Girl Service AvailableDipal Arora
 
Best Rate (Guwahati ) Call Girls Guwahati ⟟ 8617370543 ⟟ High Class Call Girl...
Best Rate (Guwahati ) Call Girls Guwahati ⟟ 8617370543 ⟟ High Class Call Girl...Best Rate (Guwahati ) Call Girls Guwahati ⟟ 8617370543 ⟟ High Class Call Girl...
Best Rate (Guwahati ) Call Girls Guwahati ⟟ 8617370543 ⟟ High Class Call Girl...Dipal Arora
 
Call Girls Ludhiana Just Call 9907093804 Top Class Call Girl Service Available
Call Girls Ludhiana Just Call 9907093804 Top Class Call Girl Service AvailableCall Girls Ludhiana Just Call 9907093804 Top Class Call Girl Service Available
Call Girls Ludhiana Just Call 9907093804 Top Class Call Girl Service AvailableDipal Arora
 
Call Girls Aurangabad Just Call 9907093804 Top Class Call Girl Service Available
Call Girls Aurangabad Just Call 9907093804 Top Class Call Girl Service AvailableCall Girls Aurangabad Just Call 9907093804 Top Class Call Girl Service Available
Call Girls Aurangabad Just Call 9907093804 Top Class Call Girl Service AvailableDipal Arora
 
VIP Hyderabad Call Girls Bahadurpally 7877925207 ₹5000 To 25K With AC Room 💚😋
VIP Hyderabad Call Girls Bahadurpally 7877925207 ₹5000 To 25K With AC Room 💚😋VIP Hyderabad Call Girls Bahadurpally 7877925207 ₹5000 To 25K With AC Room 💚😋
VIP Hyderabad Call Girls Bahadurpally 7877925207 ₹5000 To 25K With AC Room 💚😋TANUJA PANDEY
 
All Time Service Available Call Girls Marine Drive 📳 9820252231 For 18+ VIP C...
All Time Service Available Call Girls Marine Drive 📳 9820252231 For 18+ VIP C...All Time Service Available Call Girls Marine Drive 📳 9820252231 For 18+ VIP C...
All Time Service Available Call Girls Marine Drive 📳 9820252231 For 18+ VIP C...Arohi Goyal
 
Call Girls Gwalior Just Call 9907093804 Top Class Call Girl Service Available
Call Girls Gwalior Just Call 9907093804 Top Class Call Girl Service AvailableCall Girls Gwalior Just Call 9907093804 Top Class Call Girl Service Available
Call Girls Gwalior Just Call 9907093804 Top Class Call Girl Service AvailableDipal Arora
 
Russian Escorts Girls Nehru Place ZINATHI 🔝9711199012 ☪ 24/7 Call Girls Delhi
Russian Escorts Girls Nehru Place ZINATHI 🔝9711199012 ☪ 24/7 Call Girls DelhiRussian Escorts Girls Nehru Place ZINATHI 🔝9711199012 ☪ 24/7 Call Girls Delhi
Russian Escorts Girls Nehru Place ZINATHI 🔝9711199012 ☪ 24/7 Call Girls DelhiAlinaDevecerski
 
Top Quality Call Girl Service Kalyanpur 6378878445 Available Call Girls Any Time
Top Quality Call Girl Service Kalyanpur 6378878445 Available Call Girls Any TimeTop Quality Call Girl Service Kalyanpur 6378878445 Available Call Girls Any Time
Top Quality Call Girl Service Kalyanpur 6378878445 Available Call Girls Any TimeCall Girls Delhi
 
Call Girls Nagpur Just Call 9907093804 Top Class Call Girl Service Available
Call Girls Nagpur Just Call 9907093804 Top Class Call Girl Service AvailableCall Girls Nagpur Just Call 9907093804 Top Class Call Girl Service Available
Call Girls Nagpur Just Call 9907093804 Top Class Call Girl Service AvailableDipal Arora
 
The Most Attractive Hyderabad Call Girls Kothapet 𖠋 6297143586 𖠋 Will You Mis...
The Most Attractive Hyderabad Call Girls Kothapet 𖠋 6297143586 𖠋 Will You Mis...The Most Attractive Hyderabad Call Girls Kothapet 𖠋 6297143586 𖠋 Will You Mis...
The Most Attractive Hyderabad Call Girls Kothapet 𖠋 6297143586 𖠋 Will You Mis...chandars293
 
(👑VVIP ISHAAN ) Russian Call Girls Service Navi Mumbai🖕9920874524🖕Independent...
(👑VVIP ISHAAN ) Russian Call Girls Service Navi Mumbai🖕9920874524🖕Independent...(👑VVIP ISHAAN ) Russian Call Girls Service Navi Mumbai🖕9920874524🖕Independent...
(👑VVIP ISHAAN ) Russian Call Girls Service Navi Mumbai🖕9920874524🖕Independent...Taniya Sharma
 
Night 7k to 12k Navi Mumbai Call Girl Photo 👉 BOOK NOW 9833363713 👈 ♀️ night ...
Night 7k to 12k Navi Mumbai Call Girl Photo 👉 BOOK NOW 9833363713 👈 ♀️ night ...Night 7k to 12k Navi Mumbai Call Girl Photo 👉 BOOK NOW 9833363713 👈 ♀️ night ...
Night 7k to 12k Navi Mumbai Call Girl Photo 👉 BOOK NOW 9833363713 👈 ♀️ night ...aartirawatdelhi
 
Call Girls Bhubaneswar Just Call 9907093804 Top Class Call Girl Service Avail...
Call Girls Bhubaneswar Just Call 9907093804 Top Class Call Girl Service Avail...Call Girls Bhubaneswar Just Call 9907093804 Top Class Call Girl Service Avail...
Call Girls Bhubaneswar Just Call 9907093804 Top Class Call Girl Service Avail...Dipal Arora
 
VIP Call Girls Indore Kirti 💚😋 9256729539 🚀 Indore Escorts
VIP Call Girls Indore Kirti 💚😋 9256729539 🚀 Indore EscortsVIP Call Girls Indore Kirti 💚😋 9256729539 🚀 Indore Escorts
VIP Call Girls Indore Kirti 💚😋 9256729539 🚀 Indore Escortsaditipandeya
 
Call Girls Ooty Just Call 9907093804 Top Class Call Girl Service Available
Call Girls Ooty Just Call 9907093804 Top Class Call Girl Service AvailableCall Girls Ooty Just Call 9907093804 Top Class Call Girl Service Available
Call Girls Ooty Just Call 9907093804 Top Class Call Girl Service AvailableDipal Arora
 
Lucknow Call girls - 8800925952 - 24x7 service with hotel room
Lucknow Call girls - 8800925952 - 24x7 service with hotel roomLucknow Call girls - 8800925952 - 24x7 service with hotel room
Lucknow Call girls - 8800925952 - 24x7 service with hotel roomdiscovermytutordmt
 
💎VVIP Kolkata Call Girls Parganas🩱7001035870🩱Independent Girl ( Ac Rooms Avai...
💎VVIP Kolkata Call Girls Parganas🩱7001035870🩱Independent Girl ( Ac Rooms Avai...💎VVIP Kolkata Call Girls Parganas🩱7001035870🩱Independent Girl ( Ac Rooms Avai...
💎VVIP Kolkata Call Girls Parganas🩱7001035870🩱Independent Girl ( Ac Rooms Avai...Taniya Sharma
 

Último (20)

♛VVIP Hyderabad Call Girls Chintalkunta🖕7001035870🖕Riya Kappor Top Call Girl ...
♛VVIP Hyderabad Call Girls Chintalkunta🖕7001035870🖕Riya Kappor Top Call Girl ...♛VVIP Hyderabad Call Girls Chintalkunta🖕7001035870🖕Riya Kappor Top Call Girl ...
♛VVIP Hyderabad Call Girls Chintalkunta🖕7001035870🖕Riya Kappor Top Call Girl ...
 
Top Rated Bangalore Call Girls Richmond Circle ⟟ 9332606886 ⟟ Call Me For Ge...
Top Rated Bangalore Call Girls Richmond Circle ⟟ 9332606886 ⟟ Call Me For Ge...Top Rated Bangalore Call Girls Richmond Circle ⟟ 9332606886 ⟟ Call Me For Ge...
Top Rated Bangalore Call Girls Richmond Circle ⟟ 9332606886 ⟟ Call Me For Ge...
 
Call Girls Gwalior Just Call 8617370543 Top Class Call Girl Service Available
Call Girls Gwalior Just Call 8617370543 Top Class Call Girl Service AvailableCall Girls Gwalior Just Call 8617370543 Top Class Call Girl Service Available
Call Girls Gwalior Just Call 8617370543 Top Class Call Girl Service Available
 
Best Rate (Guwahati ) Call Girls Guwahati ⟟ 8617370543 ⟟ High Class Call Girl...
Best Rate (Guwahati ) Call Girls Guwahati ⟟ 8617370543 ⟟ High Class Call Girl...Best Rate (Guwahati ) Call Girls Guwahati ⟟ 8617370543 ⟟ High Class Call Girl...
Best Rate (Guwahati ) Call Girls Guwahati ⟟ 8617370543 ⟟ High Class Call Girl...
 
Call Girls Ludhiana Just Call 9907093804 Top Class Call Girl Service Available
Call Girls Ludhiana Just Call 9907093804 Top Class Call Girl Service AvailableCall Girls Ludhiana Just Call 9907093804 Top Class Call Girl Service Available
Call Girls Ludhiana Just Call 9907093804 Top Class Call Girl Service Available
 
Call Girls Aurangabad Just Call 9907093804 Top Class Call Girl Service Available
Call Girls Aurangabad Just Call 9907093804 Top Class Call Girl Service AvailableCall Girls Aurangabad Just Call 9907093804 Top Class Call Girl Service Available
Call Girls Aurangabad Just Call 9907093804 Top Class Call Girl Service Available
 
VIP Hyderabad Call Girls Bahadurpally 7877925207 ₹5000 To 25K With AC Room 💚😋
VIP Hyderabad Call Girls Bahadurpally 7877925207 ₹5000 To 25K With AC Room 💚😋VIP Hyderabad Call Girls Bahadurpally 7877925207 ₹5000 To 25K With AC Room 💚😋
VIP Hyderabad Call Girls Bahadurpally 7877925207 ₹5000 To 25K With AC Room 💚😋
 
All Time Service Available Call Girls Marine Drive 📳 9820252231 For 18+ VIP C...
All Time Service Available Call Girls Marine Drive 📳 9820252231 For 18+ VIP C...All Time Service Available Call Girls Marine Drive 📳 9820252231 For 18+ VIP C...
All Time Service Available Call Girls Marine Drive 📳 9820252231 For 18+ VIP C...
 
Call Girls Gwalior Just Call 9907093804 Top Class Call Girl Service Available
Call Girls Gwalior Just Call 9907093804 Top Class Call Girl Service AvailableCall Girls Gwalior Just Call 9907093804 Top Class Call Girl Service Available
Call Girls Gwalior Just Call 9907093804 Top Class Call Girl Service Available
 
Russian Escorts Girls Nehru Place ZINATHI 🔝9711199012 ☪ 24/7 Call Girls Delhi
Russian Escorts Girls Nehru Place ZINATHI 🔝9711199012 ☪ 24/7 Call Girls DelhiRussian Escorts Girls Nehru Place ZINATHI 🔝9711199012 ☪ 24/7 Call Girls Delhi
Russian Escorts Girls Nehru Place ZINATHI 🔝9711199012 ☪ 24/7 Call Girls Delhi
 
Top Quality Call Girl Service Kalyanpur 6378878445 Available Call Girls Any Time
Top Quality Call Girl Service Kalyanpur 6378878445 Available Call Girls Any TimeTop Quality Call Girl Service Kalyanpur 6378878445 Available Call Girls Any Time
Top Quality Call Girl Service Kalyanpur 6378878445 Available Call Girls Any Time
 
Call Girls Nagpur Just Call 9907093804 Top Class Call Girl Service Available
Call Girls Nagpur Just Call 9907093804 Top Class Call Girl Service AvailableCall Girls Nagpur Just Call 9907093804 Top Class Call Girl Service Available
Call Girls Nagpur Just Call 9907093804 Top Class Call Girl Service Available
 
The Most Attractive Hyderabad Call Girls Kothapet 𖠋 6297143586 𖠋 Will You Mis...
The Most Attractive Hyderabad Call Girls Kothapet 𖠋 6297143586 𖠋 Will You Mis...The Most Attractive Hyderabad Call Girls Kothapet 𖠋 6297143586 𖠋 Will You Mis...
The Most Attractive Hyderabad Call Girls Kothapet 𖠋 6297143586 𖠋 Will You Mis...
 
(👑VVIP ISHAAN ) Russian Call Girls Service Navi Mumbai🖕9920874524🖕Independent...
(👑VVIP ISHAAN ) Russian Call Girls Service Navi Mumbai🖕9920874524🖕Independent...(👑VVIP ISHAAN ) Russian Call Girls Service Navi Mumbai🖕9920874524🖕Independent...
(👑VVIP ISHAAN ) Russian Call Girls Service Navi Mumbai🖕9920874524🖕Independent...
 
Night 7k to 12k Navi Mumbai Call Girl Photo 👉 BOOK NOW 9833363713 👈 ♀️ night ...
Night 7k to 12k Navi Mumbai Call Girl Photo 👉 BOOK NOW 9833363713 👈 ♀️ night ...Night 7k to 12k Navi Mumbai Call Girl Photo 👉 BOOK NOW 9833363713 👈 ♀️ night ...
Night 7k to 12k Navi Mumbai Call Girl Photo 👉 BOOK NOW 9833363713 👈 ♀️ night ...
 
Call Girls Bhubaneswar Just Call 9907093804 Top Class Call Girl Service Avail...
Call Girls Bhubaneswar Just Call 9907093804 Top Class Call Girl Service Avail...Call Girls Bhubaneswar Just Call 9907093804 Top Class Call Girl Service Avail...
Call Girls Bhubaneswar Just Call 9907093804 Top Class Call Girl Service Avail...
 
VIP Call Girls Indore Kirti 💚😋 9256729539 🚀 Indore Escorts
VIP Call Girls Indore Kirti 💚😋 9256729539 🚀 Indore EscortsVIP Call Girls Indore Kirti 💚😋 9256729539 🚀 Indore Escorts
VIP Call Girls Indore Kirti 💚😋 9256729539 🚀 Indore Escorts
 
Call Girls Ooty Just Call 9907093804 Top Class Call Girl Service Available
Call Girls Ooty Just Call 9907093804 Top Class Call Girl Service AvailableCall Girls Ooty Just Call 9907093804 Top Class Call Girl Service Available
Call Girls Ooty Just Call 9907093804 Top Class Call Girl Service Available
 
Lucknow Call girls - 8800925952 - 24x7 service with hotel room
Lucknow Call girls - 8800925952 - 24x7 service with hotel roomLucknow Call girls - 8800925952 - 24x7 service with hotel room
Lucknow Call girls - 8800925952 - 24x7 service with hotel room
 
💎VVIP Kolkata Call Girls Parganas🩱7001035870🩱Independent Girl ( Ac Rooms Avai...
💎VVIP Kolkata Call Girls Parganas🩱7001035870🩱Independent Girl ( Ac Rooms Avai...💎VVIP Kolkata Call Girls Parganas🩱7001035870🩱Independent Girl ( Ac Rooms Avai...
💎VVIP Kolkata Call Girls Parganas🩱7001035870🩱Independent Girl ( Ac Rooms Avai...
 

Case study cdr p cpa re kuvan for cord november 2015

  • 1. Case Study of Common Drug Review & pan-Canadian Pharmaceutical Alliance and the first drug for PKU: restrictive criteria = no access John Adams President & CEO Canadian PKU and Allied Disorders Inc. (CanPKU) November 20, 2015 CORD Expert Patients conference
  • 2.
  • 3. PKU 101 PKU stands for Phenylketonuria: •  a rare, genetic disorder •  brain-threatening •  intellectual disabilities, seizures & other neurologic problems •  incidence in Canada: 1:12,000 •  every newborn in Canada is tested for PKU since 1960s •  only treatment since 1950s: - vegan diet without natural protein - synthetic protein (formulas & low-protein foods) - lifetime treatment, only since 2000 CanPKU Role: •  improve lives of people living with PKU and their families •  founded 2008: peer support, knowledge transfer, advocacy
  • 4. Why do we need a drug for PKU? PKU diet is very restrictive and hard to manage Francjan van Spronsen, MD, PhD, chair of scientific advisory committee of the European Society for PKU - Presenting Oct. 24, 2015
  • 5. Government Reimbursement for first drug for PKU Overview: 2010: Health Canada approves Drug company applies to CDR Drug company asks for reconsideration on seeing confidential draft report CEDC says Do Not List – special note! 2011: Provinces submit request for advice to clarify special note CEDC does not change recommendation or special note 2012: ON, SK and BC negotiate with drug company; BC in lead 2013: ON & SK list drug with strict criteria: BC drops out 2014-15: SK & ON refuse eight applications 2015: ON for pCPA says drug must go back to CDR
  • 6.
  • 7. Access to Kuvan™ today Private •  private insurance •  clinical trials •  compassionate access by drug company Governments •  Listed in ON & SK: zero patients •  Listed in QC: eight patients •  Health Canada: two patients (aboriginals) •  Alberta: two patients (disabled)
  • 9. pCPA Current Position 1.  No change in access criteria and no province will negotiate individually 2.  Drug company must submit new clinical information to CDR – fourth trip to CEDC since 2010 3.  Only if a positive CDR/CDEC recommendation, then pCPA will negotiate